Seminars in Pediatric Neurology
Volume 13, Issue 2 , Pages 121-131 , June 2006

Spinal Muscular Atrophy: From Gene to Therapy

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 Supported in part by the Deutsche Forschungsgemeinschaft, Families of SMA (USA), Initiative “Forschung und Therapie für SMA” (Germany), the Center for Molecular Medicine Cologne (CMMC), and Köln-Fortune.

PII: S1071-9091(06)00098-2

doi: 10.1016/j.spen.2006.06.008

Seminars in Pediatric Neurology
Volume 13, Issue 2 , Pages 121-131 , June 2006

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